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The Professional Network for Healthcare Experts
European Commission grants orphan designation to Vanda’s imsidolimab for generalised pustular psoriasis
The designation provides regulatory development incentives for Vanda’s IL-36 receptor inhibitor in the EU and follows orphan status for the investigational therapy in the US and Japan.
nuaxia
Aug 252 min read
FDA grants orphan drug designation to AFTX-201 for BAG3-associated dilated cardiomyopathy
The designation supports development of a one-time investigational gene therapy designed to address the underlying genetic cause of a rare form of dilated cardiomyopathy.
nuaxia
Jul 232 min read
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